Search for Clinical Trial Results
Niemann-Pick Disease Type C1 - 25 Studies Found
Status | Study |
Terminated |
Study Name: Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) Condition:
Date: 2006-12-11 Interventions:
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Completed |
Study Name: Saccadic Eye Movements in Patients With Niemann-Pick Type C Disease Condition: Niemann Pick Diseases Date: 2006-04-19 Interventions: Drug: OGT918 |
Recruiting |
Study Name: Investigating Lysosomal Storage Diseases in Minority Groups Condition:
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Completed |
Study Name: Stem Cell Transplant for Inborn Errors of Metabolism Condition:
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Completed |
Study Name: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condition:
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